AAVLK03hOTC

N/A

Report date: 2026/03/17 20:00:15

Base Information

Drug NameAAVLK03hOTC
Drug Alias NamessAAV-LK03.hAAT.hcoOTCadeno-associated viral vector serotype LK03 containing the human ornithine transcarbamylase geneBGT-OTCD
ClassificationCell and gene therapy > Gene therapy > Viral vector-based gene therapy > Adeno-associated virus vector
Mechanisms of ActionOTC gene transference
TargetsOrnithine carbamoyltransferase
Therapy Area/IndicationsOrnithine Carbamoyltransferase Deficiency Disease
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryUnited Kingdom
CombinationsNo
Global Highest StatusPhase 2 Clinical
Highest Status in ChinaN/A
Originator CompaniesBloomsbury Genetic Therapies LtdUniversity College London
China Registration ClassN/A

Develop Information

Active CompaniesUniversity College London
Inactive CompaniesN/A
Active IndicationsOrnithine Carbamoyltransferase Deficiency Disease
Inactive IndicationsN/A

Other Information

ATC CodeN/A
Related LinksN/A