AX-0422

N/A

Report date: 2026/05/09 20:00:18
NME

Base Information

Drug NameAX-0422
Drug Alias NameAX-0422AX0422
ClassificationOther
Mechanisms of ActionAlpha-L-iduronidase inhibitors
TargetsAlpha-L-iduronidase
Therapy Area/IndicationsMucopolysaccharidosis I
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryNetherlands
CombinationsNo
Global Highest StatusPreclinical
Highest Status in ChinaN/A
Originator CompaniesProqr Therapeutics Nv
China Registration ClassN/A

Develop Information

Active CompaniesProqr Therapeutics Nv
Inactive CompaniesN/A
Active IndicationsMucopolysaccharidosis I
Inactive IndicationsN/A

Other Information

ATC CodeN/A
Related LinksN/A