QR-504a

N/A

Report date: 2026/05/07 20:00:36

NME

Base Information

Drug NameQR-504a

Drug Alias NameQR-504aQR-504QRX-504QR-504a (antisense oligonucleotide RNA therapy)

ClassificationSmall molecules > Nucleosides and nucleotide derivtives > Oligonucleotide > Oligonucleotide antisense

Mechanisms of ActionGene silencingRNA interferenceRNA splicing modulators

TargetsNot applicable

Therapy Area/IndicationsFuchs' Endothelial DystrophyCorneal Diseases

Global Approved IndicationsN/A

Approved Indications in ChinaN/A

Original Approved Country/TerritoryN/A

Original Approved DateN/A

Country/TerritoryUnited Kingdom

CombinationsNo

Global Highest StatusDiscontinued (Phase 1 Clinical)

Highest Status in ChinaN/A

Originator CompaniesProqr Therapeutics

China Registration ClassN/A

Active CompaniesN/A

Active IndicationsN/A

Inactive IndicationsFuchs' Endothelial DystrophyCorneal Diseases

ATC CodeN/A