WVE-004

N/A

Report date: 2022/01/29 17:02:44
NME

Base Information

Drug NameWVE-004
Drug Alias NameC9orf72WVE-004
ClassificationSmall molecules > Nucleosides and nucleotide derivtives > Oligonucleotide > Oligonucleotide antisense
Mechanisms of ActionGuanine nucleotide exchange C9orf72 modulators
TargetsGuanine nucleotide exchange C9orf72
Therapy Area/IndicationsAmyotrophic Lateral SclerosisFrontotemporal DementiaDementia
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryBelgiumCanadaSweden +[8
CombinationsNo
Global Highest StatusPhase 2 Clinical
Highest Status in ChinaN/A
Originator CompaniesWave Life Sciences Ltd
China Registration ClassN/A

Develop Information

Inactive CompaniesN/A
Active IndicationsFrontotemporal Dementia
Inactive IndicationsAmyotrophic Lateral SclerosisDementia

Other Information

ATC CodeN/A
Related LinksN/A