AMT-150

N/A

Report date: 2024/10/22 17:09:48

Base Information

Drug NameAMT-150
Drug Alias NameAMT-150
ClassificationCell and gene therapy > Gene therapy > Viral vector-based gene therapy > Adeno-associated virus vector
Mechanisms of ActionGene silencingAtaxin-3 inhibitors
TargetsAtaxin-3
Therapy Area/IndicationsAtaxia
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryN/A
CombinationsNo
Global Highest StatusPreclinical
Highest Status in ChinaN/A
Originator CompaniesUniqure
China Registration ClassN/A

Develop Information

Active CompaniesUniqure
Inactive CompaniesN/A
Active IndicationsAtaxia
Inactive IndicationsN/A

Other Information

ATC CodeN/A
Related LinksN/A