PBCM-06

N/A

Report date: 2024/12/13 17:14:06

Base Information

Drug NamePBCM-06
Drug Alias NamePBCM-06
ClassificationCell and gene therapy > Gene therapy > Viral vector-based gene therapy > Adeno-associated virus vector
Mechanisms of ActionMitofusin-2 gene transference
TargetsMitofusin-2
Therapy Area/IndicationsCharcot-Marie-Tooth Disease
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryN/A
CombinationsNo
Global Highest StatusPreclinical
Highest Status in ChinaN/A
Originator CompaniesUniversity Of Pennsylvania
China Registration ClassN/A

Develop Information

Inactive CompaniesN/A
Active IndicationsCharcot-Marie-Tooth Disease
Inactive IndicationsN/A

Other Information

ATC CodeN/A
Related LinksN/A