AXV-101

N/A

Report date: 2025/05/09 15:53:56

Base Information

Drug NameAXV-101
Drug Alias NameAXV-101AAV9-BBS1
ClassificationCell and gene therapy > Gene therapy > Viral vector-based gene therapy > Adeno-associated virus vector
Mechanisms of ActionBBS1 gene modulators
TargetsBBSome complex member BBS1
Therapy Area/IndicationsBardet-Biedl Syndrome
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryUnited Kingdom
CombinationsNo
Global Highest StatusPreclinical
Highest Status in ChinaN/A
Originator CompaniesAxovia Therapeutics
China Registration ClassN/A

Develop Information

Active CompaniesAxovia Therapeutics
Inactive CompaniesN/A
Active IndicationsBardet-Biedl Syndrome
Inactive IndicationsN/A

Other Information

ATC CodeN/A
Related LinksN/A