MDL-201

N/A

Report date: 2025/08/29 17:06:02

Base Information

Drug NameMDL-201
Drug Alias NameMDL-201GNDM-UTRN
ClassificationCell and gene therapy > Gene therapy > Gene editing > CRISPR
Mechanisms of ActionUtrophin activators
TargetsUtrophin
Therapy Area/IndicationsMuscular Dystrophy, DuchenneMusculoskeletal Diseases
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryJapan
CombinationsNo
Global Highest StatusPreclinical
Highest Status in ChinaN/A
Originator CompaniesModalis Therapeutics Corp
China Registration ClassN/A

Develop Information

Inactive CompaniesN/A
Active IndicationsMuscular Dystrophy, DuchenneMusculoskeletal Diseases
Inactive IndicationsN/A

Other Information

ATC CodeN/A
Related LinksN/A