VTX-804

N/A

Report date: 2024/10/22 10:27:31

Base Information

Drug NameVTX-804
Drug Alias NameVTX 804VTX-804
ClassificationCell and gene therapy > Gene therapy > Viral vector-based gene therapy > Adeno-associated virus vector
Mechanisms of ActionArgininosuccinate synthase gene transference
TargetsArgininosuccinate synthase
Therapy Area/IndicationsUrea Cycle Disorders, Inborn
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryN/A
CombinationsNo
Global Highest StatusPreclinical
Highest Status in ChinaN/A
Originator CompaniesVivet Therapeutics SAS
China Registration ClassN/A

Develop Information

Active CompaniesVivet Therapeutics SAS
Inactive CompaniesN/A
Active IndicationsUrea Cycle Disorders, Inborn
Inactive IndicationsN/A

Other Information

ATC CodeN/A
Related LinksN/A