JAG-201

N/A

Report date: 2024/03/26 16:18:36

Base Information

Drug NameJAG-201
Drug Alias NameJAG 201JAG-201
ClassificationCell and gene therapy > Gene therapy > Viral vector-based gene therapy > Adeno-associated virus vector
Mechanisms of ActionSH3 and multiple ankyrin repeat domains protein 3 gene transference
TargetsSH3 and multiple ankyrin repeat domains protein 3
Therapy Area/IndicationsPhelan-McDermid syndromeAutistic DisorderAutism Spectrum Disorder
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryUnited States
CombinationsNo
Global Highest StatusPhase 1 Clinical
Highest Status in ChinaN/A
Originator CompaniesBroad Institute
China Registration ClassN/A

Develop Information

Active CompaniesJaguar Gene Therapy LLC
Inactive CompaniesN/A
Active IndicationsPhelan-McDermid syndromeAutism Spectrum Disorder
Inactive IndicationsAutistic Disorder

Other Information

ATC CodeN/A
Related LinksN/A