M-043

N/A

Report date: 2025/03/18 13:50:25

Base Information

Drug NameM-043
Drug Alias NameM-043AAV-NAGLU-S1S3Lenti-NAGLU-S1S3
ClassificationCell and gene therapy > Gene therapy > Viral vector-based gene therapy > Adeno-associated virus vector
Mechanisms of ActionAlpha-N-acetylglucosaminidase replacements
TargetsAlpha-N-acetylglucosaminidase
Therapy Area/IndicationsMucopolysaccharidosis III
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryUnited States
CombinationsNo
Global Highest StatusPreclinical
Highest Status in ChinaN/A
Originator CompaniesM6P Therapeutics Ltd
China Registration ClassN/A

Develop Information

Active CompaniesM6P Therapeutics Ltd
Inactive CompaniesN/A
Active IndicationsMucopolysaccharidosis III
Inactive IndicationsN/A

Other Information

ATC CodeN/A
Related LinksN/A