Miglustat (Beyond Batten Disease Foundation)

N/A

Report date: 2026/02/12 20:00:14

Base Information

Drug NameMiglustat (Beyond Batten Disease Foundation)
Drug Alias NameBBDF-101Batten-1
ClassificationSmall molecules > Heterocyclic drugs
Mechanisms of ActionCeramide glucosyltransferase inhibitorsAcidic alpha-glucosidase inhibitors
TargetsCeramide glucosyltransferaseAcidic alpha-glucosidase
Therapy Area/IndicationsNeuronal Ceroid-Lipofuscinoses
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryUnited States
CombinationsNo
Global Highest StatusPhase 2 Clinical
Highest Status in ChinaN/A
China Registration ClassN/A

Develop Information

Inactive CompaniesN/A
Active IndicationsNeuronal Ceroid-Lipofuscinoses
Inactive IndicationsN/A

Other Information

ATC CodeN/A
Related LinksN/A