AOC-1044

N/A

Report date: 2026/05/15 20:01:45

Base Information

Drug NameAOC-1044
Drug Alias NameDelpacibart zotadirsendel-zotaAOC-1044AOC 1044
ClassificationBiologics > Protein drugs > Immunoglobulin > Antibody > Antibody conjugate > Monoclonal antibody conjugate > Antibody-Oligonucleotide conjugate
Mechanisms of ActionRNA interferenceDystrophin expression stimulantsAnti-Transferrin receptor protein 1
TargetsDystrophinTransferrin receptor protein 1
Therapy Area/IndicationsInfant, Newborn, DiseasesGenetic Diseases, InbornNeuromuscular Diseases +[8
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryUnited States
CombinationsNo
Global Highest StatusPhase 3 Clinical
Highest Status in ChinaN/A
Originator CompaniesAvidity Biosciences Inc
China Registration ClassN/A

Develop Information

Active CompaniesAvidity Biosciences Inc
Inactive CompaniesN/A
Active IndicationsInfant, Newborn, DiseasesGenetic Diseases, InbornNeuromuscular Diseases +[6
Inactive IndicationsNervous System DiseasesMusculoskeletal Diseases

Other Information

ATC CodeN/A
Related LinksN/A