AAV-UPF1

N/A

Report date: 2025/04/08 10:17:54

Base Information

Drug NameAAV-UPF1
Drug Alias NameAAV-UPF1AAVhUPF-1
ClassificationCell and gene therapy > Gene therapy > Viral vector-based gene therapy > Adeno-associated virus vector
Mechanisms of ActionTAR DNA binding protein 43 inhibitorsGene transference
TargetsTAR DNA binding protein 43
Therapy Area/IndicationsAmyotrophic Lateral Sclerosis
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryUnited States
CombinationsNo
Global Highest StatusPreclinical
Highest Status in ChinaN/A
Originator CompaniesBrandeis University
China Registration ClassN/A

Develop Information

Active CompaniesMeiragtx Ltd
Inactive CompaniesN/A
Active IndicationsAmyotrophic Lateral Sclerosis
Inactive IndicationsN/A

Other Information

ATC CodeN/A
Related LinksN/A