PGN-EDODM1

N/A

Report date: 2026/05/07 20:00:36
NME

Base Information

Drug NamePGN-EDODM1
Drug Alias NameEDODM-1PGN-EDODM-1PGN-EDODM1
ClassificationSmall molecules > Nucleosides and nucleotide derivtives > Oligonucleotide > Peptide-oligonucleotide ConjugateSmall molecules > Synthetic peptide > Peptide drug conjugate (PDC) > Peptide-oligonucleotide ConjugateSmall molecules > Nucleosides and nucleotide derivtives > Oligonucleotide > Oligonucleotide antisense
Mechanisms of ActionRNA splicing modulatorsMuscleblind-like protein 1 inhibitorsRNA interference
TargetsMuscleblind-like protein 1
Therapy Area/IndicationsMyotonic Dystrophy
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryCanadaUnited StatesNew Zealand +[4
CombinationsNo
Global Highest StatusPhase 2 Clinical
Highest Status in ChinaN/A
Originator CompaniesPepgen Corp
China Registration ClassN/A

Develop Information

Active CompaniesPepGen IncPepgen Corp
Inactive CompaniesN/A
Active IndicationsMyotonic Dystrophy
Inactive IndicationsN/A

Other Information

ATC CodeN/A
Related LinksN/A