VAR-002

N/A

Report date: 2024/11/14 16:49:46

Base Information

Drug NameVAR-002
Drug Alias NameVAR-002
ClassificationCell and gene therapy > Gene therapy > Viral vector-based gene therapy > Adeno-associated virus vector
Mechanisms of ActionCone-rod homeobox protein gene transference
TargetsCone-rod homeobox protein
Therapy Area/IndicationsLeber Congenital AmaurosisCone-Rod Dystrophies
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryN/A
CombinationsNo
Global Highest StatusPreclinical
Highest Status in ChinaN/A
Originator CompaniesSAS Variant
China Registration ClassN/A

Develop Information

Active CompaniesSAS Variant
Inactive CompaniesN/A
Active IndicationsLeber Congenital AmaurosisCone-Rod Dystrophies
Inactive IndicationsN/A

Other Information

ATC CodeN/A
Related LinksN/A