JR-479

N/A

Report date: 2024/11/14 16:49:43

Base Information

Drug NameJR-479
Drug Alias NameBBB-penetrating βHexosaminidase A (rDNA origin) (JCR Pharmaceuticals)β-Hexosaminidase A (JCR Pharmaceuticals)
ClassificationBiologics > Protein drugs > Enzyme > Recombinant enzymeBiologics > Protein drugs > Recombinant protein > Recombinant enzyme
Mechanisms of ActionBeta-hexosaminidase subunit alpha replacementTransferrin receptor protein 1 modulators
TargetsBeta-hexosaminidase subunit alphaTransferrin receptor protein 1
Therapy Area/IndicationsGangliosidoses, GM2
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryJapan
CombinationsNo
Global Highest StatusPreclinical
Highest Status in ChinaN/A
Originator CompaniesJcr Pharmaceuticals Co Ltd
China Registration ClassN/A

Develop Information

Inactive CompaniesN/A
Active IndicationsGangliosidoses, GM2
Inactive IndicationsN/A

Other Information

ATC CodeN/A
Related LinksN/A