PRX-ASS1

N/A

Report date: 2024/12/18 13:39:48

Base Information

Drug NamePRX-ASS1
Drug Alias NameN/A
ClassificationCell and gene therapy > Gene therapy > mRNA
Mechanisms of ActionEnzyme replacements
TargetsUpdating
Therapy Area/IndicationsUrea Cycle Disorders, Inborn
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryUnited States
CombinationsNo
Global Highest StatusPending (Preclinical)
Highest Status in ChinaN/A
Originator CompaniesPhaseRx Inc
China Registration ClassN/A

Develop Information

Active CompaniesN/A
Inactive CompaniesPhaseRx Inc
Active IndicationsN/A
Inactive IndicationsUrea Cycle Disorders, Inborn

Other Information

ATC CodeN/A
Related LinksN/A