rAAVrh74.MCK.Micro-Dystrophin (Sarepta Therapeutics Inc)

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Report date: 2024/12/23 11:01:52

Base Information

Drug NamerAAVrh74.MCK.Micro-Dystrophin (Sarepta Therapeutics Inc)
Drug Alias NameAAVrh74.MHCK7.micro dystrophin
ClassificationCell and gene therapy > Gene therapy > Viral vector-based gene therapy > Adeno-associated virus vector > AAVrh74 vector
Mechanisms of ActionDysferlin gene transference
TargetsDysferlin
Therapy Area/IndicationsMuscular Dystrophy, Duchenne
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryN/A
CombinationsNo
Global Highest StatusPhase 2 Clinical
Highest Status in ChinaN/A
Originator CompaniesSarepta Therapeutics Inc
China Registration ClassN/A

Develop Information

Active CompaniesSarepta Therapeutics IncNationwide Children'S Hospital
Inactive CompaniesN/A
Active IndicationsMuscular Dystrophy, Duchenne
Inactive IndicationsN/A

Other Information

ATC CodeN/A
Related LinksN/A