BCKDHA mRNA therapy (Moderna)

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Report date: 2025/02/01 20:00:06
NME

Base Information

Drug NameBCKDHA mRNA therapy (Moderna)
Drug Alias Nameliver-directed lipid nanoparticle mRNA therapy (Moderna)
ClassificationSmall molecules > Nucleosides and nucleotide derivtives > OligonucleotideSmall molecules > Lipid
Mechanisms of ActionBranched-chain alpha-ketoacid dehydrogenase kinase stimulants
TargetsBranched-chain alpha-ketoacid dehydrogenase kinase
Therapy Area/IndicationsMaple Syrup Urine Disease
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryUnited States
CombinationsNo
Global Highest StatusPending (Preclinical)
Highest Status in ChinaN/A
Originator CompaniesModerna Inc
China Registration ClassN/A

Develop Information

Active CompaniesN/A
Inactive CompaniesModerna Inc
Active IndicationsN/A
Inactive IndicationsMaple Syrup Urine Disease

Other Information

ATC CodeN/A
Related LinksN/A