BGT-NPC

N/A

Report date: 2025/01/26 19:23:22

Base Information

Drug NameBGT-NPC

Drug Alias Nameadeno-associated viral vector 9-based gene therapy(UCL/Bloomsbury Genetic Therapies)AAV9-NPC gene therapy (UCL/Bloomsbury Genetic Therapies)BGT-NPC

ClassificationBiologics

Mechanisms of ActionNPC Intracellular Cholesterol Transporter 1 modulators

TargetsNPC Intracellular Cholesterol Transporter 1

Therapy Area/IndicationsNiemann-Pick Disease, Type C

Global Approved IndicationsN/A

Approved Indications in ChinaN/A

Original Approved Country/TerritoryN/A

Original Approved DateN/A

Country/TerritoryUnited StatesEuropeUnited Kingdom

CombinationsNo

Global Highest StatusPreclinical

Highest Status in ChinaN/A

Originator CompaniesUniversity College London

China Registration ClassN/A

Develop Information

Active CompaniesBloomsbury Genetic Therapies Ltd

Inactive CompaniesN/A

Active IndicationsNiemann-Pick Disease, Type C

Inactive IndicationsN/A

Other Information

ATC CodeN/A