bifunctional lentivirus-based gene therapy (Genethon/INSERM/University of Modena and Reggio Emilia/Assistance Publique-Hopitaux de Paris)

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Report date: 2025/01/26 19:23:31

Base Information

Drug Namebifunctional lentivirus-based gene therapy (Genethon/INSERM/University of Modena and Reggio Emilia/Assistance Publique-Hopitaux de Paris)
Drug Alias Nameanti-sickling beta globin transgene therapy (Genethon/INSERM/University of Modena and Reggio Emilia/Assistance Publique-Hopitaux de Paris)beta-AS/amiR-LVBCL11A gene silencing lentivirus-based gene therapy (Genethon/INSERM/University of Modena and Reggio Emilia/Assistance Publique-Hopitaux de Paris)
ClassificationOther
Mechanisms of ActionBCL11A gene inhibitorsHemoglobin beta chain stimulants
TargetsHemoglobin beta chainB-cell lymphoma/leukemia 11A
Therapy Area/IndicationsHemoglobinopathies
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryFrance
CombinationsNo
Global Highest StatusPreclinical
Highest Status in ChinaN/A
Originator CompaniesGenethon
China Registration ClassN/A

Develop Information

Inactive CompaniesN/A
Active IndicationsHemoglobinopathies
Inactive IndicationsN/A

Other Information

ATC CodeN/A
Related LinksN/A