ATP7B gene therapy (MeiraGTx)

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Report date: 2025/01/26 19:29:43

Base Information

Drug NameATP7B gene therapy (MeiraGTx)
Drug Alias NameAAV-ATP7B opti
ClassificationBiologics
Mechanisms of ActionCopper-transporting ATPase 2 gene transference
TargetsCopper-transporting ATPase 2
Therapy Area/IndicationsHepatolenticular Degeneration
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryUnited States
CombinationsNo
Global Highest StatusPreclinical
Highest Status in ChinaN/A
Originator CompaniesMeiragtx Ltd
China Registration ClassN/A

Develop Information

Active CompaniesMeiragtx Ltd
Inactive CompaniesN/A
Active IndicationsHepatolenticular Degeneration
Inactive IndicationsN/A

Other Information

ATC CodeN/A
Related LinksN/A