ATP7B gene therapy (Generation Bio)

N/A

Report date: 2025/01/26 19:29:45
NME

Base Information

Drug NameATP7B gene therapy (Generation Bio)
Drug Alias NameceDNA construct gene therapy (Generation Bio)closed-ended DNA construct gene therapy (Generation Bio)
ClassificationSmall molecules > Nucleosides and nucleotide derivtives > Oligonucleotide
Mechanisms of ActionCopper-transporting ATPase 2 gene transference
TargetsCopper-transporting ATPase 2
Therapy Area/IndicationsHepatolenticular Degeneration
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryUnited States
CombinationsNo
Global Highest StatusPreclinical
Highest Status in ChinaN/A
Originator CompaniesGeneration Bio Co
China Registration ClassN/A

Develop Information

Active CompaniesGeneration Bio Co
Inactive CompaniesN/A
Active IndicationsHepatolenticular Degeneration
Inactive IndicationsN/A

Other Information

ATC CodeN/A
Related LinksN/A