ATSN-301

N/A

Report date: 2025/01/26 19:29:54

Base Information

Drug NameATSN-301
Drug Alias NameAAV-MYO7A gene therapy (Atsena Therapeutics)USH1B gene therapy (Atsena Therapeutic)ATSN-301
ClassificationBiologics
Mechanisms of ActionMyosin VIIA Gene transference
TargetsMyosin VIIA
Therapy Area/IndicationsBlindnessUsher Syndromes
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryUnited States
CombinationsNo
Global Highest StatusPreclinical
Highest Status in ChinaN/A
Originator CompaniesAtsena Therapeutics
China Registration ClassN/A

Develop Information

Active CompaniesAtsena Therapeutics
Inactive CompaniesN/A
Active IndicationsBlindnessUsher Syndromes
Inactive IndicationsN/A

Other Information

ATC CodeN/A
Related LinksN/A