autologous hematopoietic stem cells transduced with Factor IX (Discovery genomics)

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Report date: 2025/02/01 20:00:06

Base Information

Drug Nameautologous hematopoietic stem cells transduced with Factor IX (Discovery genomics)
Drug Alias Namehematopoietic Factor IX gene therapy (Discovery genomics)
ClassificationCell and gene therapy > Cell therapy > Stem cell therapy > Hematopoietic stem cells therapy
Mechanisms of ActionCoagulation factor IX stimulants
TargetsCoagulation factor IX
Therapy Area/IndicationsHemophilia B
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryUnited States
CombinationsNo
Global Highest StatusPending (Preclinical)
Highest Status in ChinaN/A
Originator CompaniesDiscovery Genomics Inc
China Registration ClassN/A

Develop Information

Active CompaniesN/A
Inactive CompaniesDiscovery Genomics Inc
Active IndicationsN/A
Inactive IndicationsHemophilia B

Other Information

ATC CodeN/A
Related LinksN/A