CNS-2 (Lacerta Therapeutics)

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Report date: 2025/01/26 16:41:42

Base Information

Drug NameCNS-2 (Lacerta Therapeutics)
Drug Alias NameCNS-2 (Sarepta/Lactera)AADC deficiency gene therapy (Lacerta/Sarepta)hAADC gene therapy (Lacerta/Sarepta)L-amino acid decarboxylase deficiency gene therapy (Sarepta/Lacerta)
ClassificationBiologics
Mechanisms of ActionUpdating
TargetsUpdating
Therapy Area/Indications +[1N/A
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryUnited States
CombinationsNo
Global Highest StatusPreclinical
Highest Status in ChinaN/A
Originator CompaniesLacerta Therapeutics Inc
China Registration ClassN/A

Develop Information

Active CompaniesLacerta Therapeutics Inc
Inactive CompaniesSarepta Therapeutics Inc
Active Indications +[1N/A
Inactive IndicationsN/A

Other Information

ATC CodeN/A
Related LinksN/A