CRISPR/Cas9-gene therapy (Casebia)

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Report date: 2025/01/26 18:07:57

Base Information

Drug NameCRISPR/Cas9-gene therapy (Casebia)
Drug Alias NameN/A
ClassificationBiologics
Mechanisms of ActionCoagulation factor IX stimulants
TargetsCoagulation factor IX
Therapy Area/IndicationsHemophilia B
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryUnited States
CombinationsNo
Global Highest StatusPreclinical
Highest Status in ChinaN/A
Originator CompaniesCasebia Therapeutics Llc
China Registration ClassN/A

Develop Information

Active CompaniesCasebia Therapeutics Llc
Inactive CompaniesN/A
Active IndicationsHemophilia B
Inactive IndicationsN/A

Other Information

ATC CodeN/A
Related LinksN/A