C9orf72-FTD

N/A

Report date: 2025/08/15 17:43:03

Base Information

Drug NameC9orf72-FTD
Drug Alias NameAAV-RCas13d (Locana)C9orf72 CRISPR/Cas13d (LocanaBio)RNA-targeting gene therapy (Locana)C9orf72-targeting RCas13d (Locana)
ClassificationCell and gene therapy > Gene therapy > Gene editing > CRISPR > CRISPR-Cas13Cell and gene therapy > Gene therapy > Viral vector-based gene therapy > Adeno-associated virus vector
Mechanisms of ActionGuanine nucleotide exchange C9orf72 modulators
TargetsGuanine nucleotide exchange C9orf72
Therapy Area/IndicationsFrontotemporal Dementia
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryUnited States
CombinationsNo
Global Highest StatusPreclinical
Highest Status in ChinaN/A
Originator CompaniesLocanabio Inc
China Registration ClassN/A

Develop Information

Active CompaniesLocanabio Inc
Inactive CompaniesN/A
Active IndicationsFrontotemporal Dementia
Inactive IndicationsN/A

Other Information

ATC CodeN/A
Related LinksN/A