CFTR gene therapy (Prime Medicine)

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Report date: 2025/12/12 17:32:43

Base Information

Drug NameCFTR gene therapy (Prime Medicine)
Drug Alias NameN/A
ClassificationCell and gene therapy > Gene therapy > Gene editing
Mechanisms of ActionCystic fibrosis transmembrane conductance regulator stimulants
TargetsCystic fibrosis transmembrane conductance regulator
Therapy Area/IndicationsCystic Fibrosis
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryUnited States
CombinationsNo
Global Highest StatusPreclinical
Highest Status in ChinaN/A
Originator CompaniesPrime Medicine Inc
China Registration ClassN/A

Develop Information

Active CompaniesPrime Medicine Inc
Inactive CompaniesN/A
Active IndicationsCystic Fibrosis
Inactive IndicationsN/A

Other Information

ATC CodeN/A
Related LinksN/A