dysferlin gene therapy (Atamyo)

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Report date: 2025/01/26 16:27:12

Base Information

Drug Namedysferlin gene therapy (Atamyo)
Drug Alias NameDYSF gene therapy (Atamyo)dysferlin gene therapy (Genethon)dysferlin gene-containing recombinant AAV vector based therapy (Genethon)
ClassificationBiologics
Mechanisms of ActionDysferlin gene transference
TargetsDysferlin
Therapy Area/IndicationsMuscular Dystrophies, Limb-GirdleMuscular Diseases
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryFrance
CombinationsNo
Global Highest StatusPreclinical
Highest Status in ChinaN/A
Originator CompaniesGenethon
China Registration ClassN/A

Develop Information

Active CompaniesAtamyo Therapeutics SAS
Inactive CompaniesGenethon
Active IndicationsMuscular Dystrophies, Limb-Girdle
Inactive IndicationsMuscular Diseases

Other Information

ATC CodeN/A
Related LinksN/A