ENZ-001

N/A

Report date: 2025/01/26 19:24:34

Base Information

Drug NameENZ-001
Drug Alias Nameartificial site-specific RNA endonuclease (Enzerna Biosciences)ENZ-001
ClassificationBiologics
Mechanisms of ActionMyotonin-protein kinase modulators
TargetsMyotonin-protein kinase
Therapy Area/IndicationsCorneal dystrophySpinocerebellar AtaxiasMyotonic Dystrophy
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryUnited States
CombinationsNo
Global Highest StatusPreclinical
Highest Status in ChinaN/A
China Registration ClassN/A

Develop Information

Inactive CompaniesN/A
Active IndicationsCorneal dystrophySpinocerebellar AtaxiasMyotonic Dystrophy
Inactive IndicationsN/A

Other Information

ATC CodeN/A
Related LinksN/A