ET-9

N/A

Report date: 2025/01/26 17:00:48

Base Information

Drug NameET-9
Drug Alias NameAAV3-based Factor IX gene therapy (Expression Therapeutics/Fudan University/University of Florida/Emory University/Indiana University School of Medicine)Factor IX gene therapy (Expression Therapeutics/Fudan University/University of Florida/Emory University/Indiana University School of Medicine)Factor IX gene therapy (Expression Therapeutics/Fudan University/University of Florida/Emory University/Indiana University School of Medicine)scAAV3-HSh-TTR-Padua-FIX-LCOET-9
ClassificationBiologics
Mechanisms of ActionCoagulation factor IX stimulants
TargetsCoagulation factor IX
Therapy Area/IndicationsHemophilia B
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryUnited States
CombinationsNo
Global Highest StatusPreclinical
Highest Status in ChinaN/A
Originator CompaniesEmory University
China Registration ClassN/A

Develop Information

Inactive CompaniesN/A
Active IndicationsHemophilia B
Inactive IndicationsN/A

Other Information

ATC CodeN/A
Related LinksN/A