DMD gene therapy (Scriptr/CANbridge Pharmaceuticals)

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Report date: 2025/01/26 19:12:47

Base Information

Drug NameDMD gene therapy (Scriptr/CANbridge Pharmaceuticals)
Drug Alias NameDMD gene therapy (Scriptr/CANbridge Pharmaceuticals)
ClassificationBiologics
Mechanisms of ActionDystrophin expression stimulants
TargetsDystrophin
Therapy Area/IndicationsMuscular Dystrophy, Duchenne
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryUnited StatesMainland China
CombinationsNo
Global Highest StatusPreclinical
Highest Status in ChinaPreclinical
Originator CompaniesScriptr Global Inc
China Registration ClassN/A

Develop Information

Inactive CompaniesN/A
Active IndicationsMuscular Dystrophy, Duchenne
Inactive IndicationsN/A

Other Information

ATC CodeN/A
Related LinksN/A