antisense oligonucleotide (Ionis Pharmaceuticals/Rosalind Franklin University of Medicine and Science)

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Report date: 2025/01/26 17:08:22
NME

Base Information

Drug Nameantisense oligonucleotide (Ionis Pharmaceuticals/Rosalind Franklin University of Medicine and Science)
Drug Alias NameCLN3 antisense oligonucleotide exon skipping therapy (Ionis Pharmaceuticals)CLN3 splice-switching antisense oligonucleotide therapy (Ionis Pharmaceuticals)CLN3 antisense oligonucleotide (Ionis Pharmaceuticals/Rosalind Franklin University of Medicine and Science)SSO-26
ClassificationSmall molecules > Nucleosides and nucleotide derivtives > Oligonucleotide > Oligonucleotide antisense
Mechanisms of ActionBattenin modulators
TargetsBattenin
Therapy Area/IndicationsNeuronal Ceroid-Lipofuscinoses
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryUnited States
CombinationsNo
Global Highest StatusPreclinical
Highest Status in ChinaN/A
Originator CompaniesRosalind Franklin University Of Medicine And Science
China Registration ClassN/A

Develop Information

Active CompaniesIonis Pharmaceuticals IncRosalind Franklin University Of Medicine And Science
Inactive CompaniesN/A
Active IndicationsNeuronal Ceroid-Lipofuscinoses
Inactive IndicationsN/A

Other Information

ATC CodeN/A
Related LinksN/A