AL-00804

N/A

Report date: 2025/01/26 18:09:43
NME

Base Information

Drug NameAL-00804
Drug Alias NameGlucosylceramide Synthase Inhibitor (AceLink Therapeutics)AL-00804
ClassificationSmall molecules > Heterocyclic drugs
Mechanisms of ActionCeramide glucosyltransferase inhibitors
TargetsCeramide glucosyltransferase
Therapy Area/IndicationsLysosomal Storage DiseasesGaucher DiseaseGangliosidosis, GM1 +[7
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryUnited States
CombinationsNo
Global Highest StatusPreclinical
Highest Status in ChinaN/A
Originator CompaniesAceLink Therapeutics Inc
China Registration ClassN/A

Develop Information

Active CompaniesAceLink Therapeutics Inc
Inactive CompaniesN/A
Active IndicationsLysosomal Storage DiseasesGaucher DiseaseGangliosidosis, GM1 +[7
Inactive IndicationsN/A

Other Information

ATC CodeN/A
Related LinksN/A