alpha-glucosidase gene therapy (Applied Genetic Technologies)

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Report date: 2025/02/01 20:00:06

Base Information

Drug Namealpha-glucosidase gene therapy (Applied Genetic Technologies)
Drug Alias NamerAAV-GAA (Applied Genetic Technologies)
ClassificationBiologics
Mechanisms of ActionAcidic alpha-glucosidase modulators
TargetsAcidic alpha-glucosidase
Therapy Area/IndicationsGlycogen Storage Disease Type II
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryUnited States
CombinationsNo
Global Highest StatusPending (Preclinical)
Highest Status in ChinaN/A
Originator CompaniesBeacon Therapeutics Holdings Ltd
China Registration ClassN/A

Develop Information

Active CompaniesN/A
Inactive CompaniesBeacon Therapeutics Holdings Ltd
Active IndicationsN/A
Inactive IndicationsGlycogen Storage Disease Type II

Other Information

ATC CodeN/A
Related LinksN/A