Anc80L65-ARSA

N/A

Report date: 2025/01/26 19:06:49

Base Information

Drug NameAnc80L65-ARSA
Drug Alias NameARSA gene therapy (Affinia Therapeutics)AFTX-001
ClassificationBiologics
Mechanisms of ActionARSA gene transference
TargetsCerebroside-sulfatase
Therapy Area/IndicationsLeukodystrophy, Metachromatic
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryUnited States
CombinationsNo
Global Highest StatusPreclinical
Highest Status in ChinaN/A
Originator CompaniesAffinia Therapeutics Inc
China Registration ClassN/A

Develop Information

Active CompaniesAffinia Therapeutics Inc
Inactive CompaniesN/A
Active IndicationsLeukodystrophy, Metachromatic
Inactive IndicationsN/A

Other Information

ATC CodeN/A
Related LinksN/A