HTX-001

N/A

Report date: 2026/05/21 09:33:28
NME

Base Information

Drug NameHTX-001
Drug Alias NameWisper long non-coding RNA-targeted antisense oligonucleotide (HAYA Therapeutics)HTX-001
ClassificationSmall molecules > Nucleosides and nucleotide derivtives > Oligonucleotide > Oligonucleotide antisense
Mechanisms of ActionUpdating
TargetsUpdating
Therapy Area/IndicationsCardiomyopathy, Hypertrophic
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritorySwitzerland
CombinationsNo
Global Highest StatusPhase 1 Clinical
Highest Status in ChinaN/A
Originator CompaniesHAYA Therapeutics SA
China Registration ClassN/A

Develop Information

Active CompaniesHAYA Therapeutics SA
Inactive CompaniesN/A
Active IndicationsCardiomyopathy, Hypertrophic
Inactive IndicationsN/A

Other Information

ATC CodeN/A
Related LinksN/A