human iduronate 2-sulfatase stem cell-based gene therapy (University of Padua)

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Report date: 2025/01/26 15:33:17

Base Information

Drug Namehuman iduronate 2-sulfatase stem cell-based gene therapy (University of Padua)

Drug Alias NameIDS-transduced autologous CD34-positive hematopoietic stem cell therapy (University of Padua)human IDS stem cell-based gene therapy (University of Padua)human iduronate 2-sulfatase gene therapy (University of Padua)

ClassificationCell and gene therapy > Cell therapy > Stem cell therapy > Hematopoietic stem cells therapy

Mechanisms of ActionIduronate-2-sulfatase gene transference

TargetsIduronate-2-sulfatase

Therapy Area/IndicationsMucopolysaccharidosis II

Global Approved IndicationsN/A

Approved Indications in ChinaN/A

Original Approved Country/TerritoryN/A

Original Approved DateN/A

Country/TerritoryEurope

CombinationsNo

Global Highest StatusPreclinical

Highest Status in ChinaN/A

Originator CompaniesUniversity Of Padova

China Registration ClassN/A

Develop Information

Active CompaniesUniversity Of Padova

Inactive CompaniesN/A

Active IndicationsMucopolysaccharidosis II

Inactive IndicationsN/A

Other Information

ATC CodeN/A