Human methylmalonyl-CoA mutase gene therapy (Parexel International)

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Report date: 2025/01/26 18:00:24

Base Information

Drug NameHuman methylmalonyl-CoA mutase gene therapy (Parexel International)
Drug Alias Nameadeno-associated viral vector LK03 encoding human methylmalonyl-CoA mutase (Parexel)
ClassificationBiologics
Mechanisms of ActionMethylmalonyl-CoA Mutase modulators
TargetsMethylmalonyl-CoA Mutase
Therapy Area/IndicationsMethylmalonic acidaemia
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryIreland
CombinationsNo
Global Highest StatusPreclinical
Highest Status in ChinaN/A
Originator CompaniesParexel International Corp
China Registration ClassN/A

Develop Information

Inactive CompaniesN/A
Active IndicationsMethylmalonic acidaemia
Inactive IndicationsN/A

Other Information

ATC CodeN/A
Related LinksN/A