GNT-0008

N/A

Report date: 2025/01/26 15:51:44
NME

Base Information

Drug NameGNT-0008
Drug Alias Namecalpain-3 gene therapy (Genethon)GNT-0008
ClassificationSmall molecules > Nucleosides and nucleotide derivtives > Oligonucleotide
Mechanisms of ActionCalpain-3 stimulants
TargetsCalpain-3
Therapy Area/IndicationsMuscular Dystrophies, Limb-Girdle
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryUnited StatesFrance
CombinationsNo
Global Highest StatusPreclinical
Highest Status in ChinaN/A
Originator CompaniesGenethon
China Registration ClassN/A

Develop Information

Active CompaniesAtamyo Therapeutics SAS
Inactive CompaniesGenethon
Active IndicationsMuscular Dystrophies, Limb-Girdle
Inactive IndicationsN/A

Other Information

ATC CodeN/A
Related LinksN/A