GTDF-100

N/A

Report date: 2025/01/26 17:28:54

Base Information

Drug NameGTDF-100
Drug Alias NameDYSF gene therapy (Genotarget/Human Stem Cells Institute/North-Western State Medical University/Belgorod State University)rAAV-DYSFGTDF-100
ClassificationBiologics
Mechanisms of ActionDysferlin gene transference
TargetsDysferlin
Therapy Area/IndicationsMuscular Dystrophies, Limb-GirdleMuscular Diseases
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryRussian Federation
CombinationsNo
Global Highest StatusPreclinical
Highest Status in ChinaN/A
Originator CompaniesHuman Stem Cells Institute
China Registration ClassN/A

Develop Information

Inactive CompaniesN/A
Active IndicationsMuscular Dystrophies, Limb-GirdleMuscular Diseases
Inactive IndicationsN/A

Other Information

ATC CodeN/A
Related LinksN/A