GTFP-100

N/A

Report date: 2025/01/26 18:49:05

Base Information

Drug NameGTFP-100
Drug Alias NameFKRP gene therapy (Genotarget)GTFP-100
ClassificationBiologics
Mechanisms of ActionRibitol 5-phosphate transferase FKRP inhibitors
TargetsRibitol 5-phosphate transferase FKRP
Therapy Area/IndicationsMuscular Dystrophies
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryRussian Federation
CombinationsNo
Global Highest StatusPreclinical
Highest Status in ChinaN/A
Originator CompaniesGenotarget LLC
China Registration ClassN/A

Develop Information

Active CompaniesGenotarget LLC
Inactive CompaniesN/A
Active IndicationsMuscular Dystrophies
Inactive IndicationsN/A

Other Information

ATC CodeN/A
Related LinksN/A