GYS1 oligonucleotide antisense inhibitor (Entrada Therapeutics)

N/A

Report date: 2025/01/26 18:55:36
NME

Base Information

Drug NameGYS1 oligonucleotide antisense inhibitor (Entrada Therapeutics)
Drug Alias NameN/A
ClassificationSmall molecules > Nucleosides and nucleotide derivtives > Oligonucleotide
Mechanisms of ActionGlycogen synthase 1 inhibitors
TargetsGlycogen synthase 1
Therapy Area/IndicationsNeuromuscular DiseasesGlycogen Storage Disease Type II
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryUnited States
CombinationsNo
Global Highest StatusPreclinical
Highest Status in ChinaN/A
Originator CompaniesEntrada Therapeutics Inc
China Registration ClassN/A

Develop Information

Active CompaniesEntrada Therapeutics Inc
Inactive CompaniesN/A
Active IndicationsNeuromuscular DiseasesGlycogen Storage Disease Type II
Inactive IndicationsN/A

Other Information

ATC CodeN/A
Related LinksN/A