HBB gene editing therapy (Trucode Gene)

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Report date: 2025/02/01 20:00:06
NME

Base Information

Drug NameHBB gene editing therapy (Trucode Gene)
Drug Alias Namehemoglobin subunit beta gene editing therapy (Trucode Gene)
ClassificationSmall molecules > Nucleosides and nucleotide derivtives > Oligonucleotide
Mechanisms of ActionHemoglobin beta chain stimulants
TargetsHemoglobin beta chain
Therapy Area/Indicationsbeta-ThalassemiaAnemia, Sickle Cell
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryUnited States
CombinationsNo
Global Highest StatusPending (Preclinical)
Highest Status in ChinaN/A
Originator CompaniesTrucode Gene Repair Inc
China Registration ClassN/A

Develop Information

Active CompaniesN/A
Inactive CompaniesTrucode Gene Repair Inc
Active IndicationsN/A
Inactive Indicationsbeta-ThalassemiaAnemia, Sickle Cell

Other Information

ATC CodeN/A
Related LinksN/A