FMR1 gene therapy (Taysha Gene Therapies/University of Toronto/University of Texas Southwestern Medical Center)

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Report date: 2025/01/26 18:29:59

Base Information

Drug NameFMR1 gene therapy (Taysha Gene Therapies/University of Toronto/University of Texas Southwestern Medical Center)
Drug Alias NameAAV9-based FMR1 gene therapy (Taysha Gene Therapies/University of Toronto/University of Texas Southwestern Medical Center)scAAV-JeT-hFMR1iso17
ClassificationBiologics
Mechanisms of ActionFragile X Messenger Ribonucleoprotein 1 modulators
TargetsFragile X Messenger Ribonucleoprotein 1
Therapy Area/IndicationsFragile X Syndrome
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryCanadaUnited States
CombinationsNo
Global Highest StatusPreclinical
Highest Status in ChinaN/A
Originator CompaniesUniversity of Toronto
China Registration ClassN/A

Develop Information

Inactive CompaniesN/A
Active IndicationsFragile X Syndrome
Inactive IndicationsN/A

Other Information

ATC CodeN/A
Related LinksN/A