GALT gene therapy (Pfizer)

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Report date: 2025/01/26 19:02:08

Base Information

Drug NameGALT gene therapy (Pfizer)
Drug Alias NameAAV2-GALT gene therapy (Pfizer)
ClassificationBiologics
Mechanisms of ActionGalactose-1-phosphate uridylyltransferase gene transference
TargetsGalactose-1-phosphate uridylyltransferase
Therapy Area/IndicationsGalactosemias
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryUnited States
CombinationsNo
Global Highest StatusPreclinical
Highest Status in ChinaN/A
Originator CompaniesPfizer Inc
China Registration ClassN/A

Develop Information

Active CompaniesPfizer Inc
Inactive CompaniesN/A
Active IndicationsGalactosemias
Inactive IndicationsN/A

Other Information

ATC CodeN/A
Related LinksN/A