GALT gene therapy (Radboud UMC/Moderna/University of Utah/Maastricht University Medical Center)

N/A

Report date: 2025/01/26 17:50:11
NME

Base Information

Drug NameGALT gene therapy (Radboud UMC/Moderna/University of Utah/Maastricht University Medical Center)
Drug Alias NameGALT mRNA therapy (Radboud UMC/Moderna/University of Utah/Maastricht University Medical Center)
ClassificationSmall molecules > Nucleosides and nucleotide derivtives > Oligonucleotide
Mechanisms of ActionGalactose-1-phosphate uridylyltransferase gene transference
TargetsGalactose-1-phosphate uridylyltransferase
Therapy Area/IndicationsGalactosemias
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryUnited StatesNetherlands
CombinationsNo
Global Highest StatusPreclinical
Highest Status in ChinaN/A
Originator CompaniesThe University Of Utah
China Registration ClassN/A

Develop Information

Active CompaniesMaastricht University Medical CenterRadboud Centre for Mitochondrial MedicineModerna Inc +[4] 
Inactive CompaniesN/A
Active IndicationsGalactosemias
Inactive IndicationsN/A

Other Information

ATC CodeN/A
Related LinksN/A