GD-AAV8

N/A

Report date: 2025/02/01 20:00:06

Base Information

Drug NameGD-AAV8
Drug Alias NameGaucher disease gene therapy (Regenx Biosciences)adeno-associated virus vector 8 based gene therapy (RegenX Biosciences)GD-AAV8
ClassificationBiologics
Mechanisms of ActionGlucosylceramidase stimulants
TargetsGlucosylceramidase
Therapy Area/IndicationsGaucher Disease
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryUnited States
CombinationsNo
Global Highest StatusPending (Preclinical)
Highest Status in ChinaN/A
Originator CompaniesRegenxbio Inc
China Registration ClassN/A

Develop Information

Active CompaniesN/A
Inactive CompaniesRegenxbio Inc
Active IndicationsN/A
Inactive IndicationsGaucher Disease

Other Information

ATC CodeN/A
Related LinksN/A